Salima Hacein-Bey-Abina
- Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
2010/09/01 by Marina Cavazzana-Calvo, Marina Cavazzana, Emmanuel Payen +47 · 8 citations
Biochemistry, Genetics and Molecular Biology · Medicine · #Allele #Biology #Blood transfusion #Gene #Genetic enhancement #Genetics #Haematopoiesis #Hemoglobinopathies and Related Disorders #Immunology #RNA Interference and Gene Delivery #Stem cell #Thalassemia #Transfusion therapy #Viral vector #Virus-based gene therapy research
- Gene Therapy in Patients with Transfusion-Dependent β-Thalassemia
2018/04/18 by Alexis A. Thompson, Mark C. Walters, Janet L. Kwiatkowski +54 · 29 citations
Medicine · #Biology #Blood transfusion #Erythrocyte Function and Pathophysiology #Gene #Genetic enhancement #Genetics #Hemoglobinopathies and Related Disorders #Internal medicine #Medicine #Parvovirus B19 Infection Studies #Thalassemia #Transfusion therapy
- Gene Therapy in a Patient with Sickle Cell Disease
2017/03/01 by Jean‐Antoine Ribeil, Jean-Antoine Ribeil, Salima Hacein‐Bey‐Abina +33 · 30 citations
Biochemistry, Genetics and Molecular Biology · Medicine · #Adverse effect #Biology #Busulfan #Disease #Gene #Genetic enhancement #Genetics #Globin #Hematopoietic stem cell transplantation #Hemoglobin #Hemoglobinopathies and Related Disorders #Hemoglobinopathy #Immunology #Internal medicine #Medicine #Missense mutation #Mutation #Parvovirus B19 Infection Studies #Recombinant DNA #Sickle cell anemia #Viral vector #Virus-based gene therapy research
- 20 years of gene therapy for SCID
2010/05/18 by Alain Fischer, Salima Hacein-Bey-Abina, Salima Hacein‐Bey‐Abina +2 · 5 citations
Biochemistry, Genetics and Molecular Biology · Medicine · #CAR-T cell therapy research #RNA Interference and Gene Delivery #Virus-based gene therapy research