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Emmanuel Payen

  1. Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
    2010/09/01 by Marina Cavazzana, Marina Cavazzana-Calvo, Emmanuel Payen +47 · 1,273 citations
    Biochemistry, Genetics and Molecular Biology · Medicine · #Allele #Biology #Blood transfusion #Gene #Genetic enhancement #Genetics #Haematopoiesis #Hemoglobinopathies and Related Disorders #Immunology #RNA Interference and Gene Delivery #Stem cell #Thalassemia #Transfusion therapy #Viral vector #Virus-based gene therapy research