Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1

2006/04/01 by Marion G Ott, Marion Ott, Manfred Schmidt +31 · 10 citations
Biochemistry, Genetics and Molecular Biology · Immunology and Microbiology · Medicine · #Biology #Bone marrow #CAR-T cell therapy research #Cancer research #Chronic granulomatous disease #Gene #Genetic enhancement #Genetics #Haematopoiesis #Immune system #Immunology #Medicine #Myeloid #Myelopoiesis #Neutrophil, Myeloperoxidase and Oxidative Mechanisms #Primary immunodeficiency #Severe combined immunodeficiency #Stem cell #Virus-based gene therapy research

paper · doi:10.1038/nm1393

crossref issued 2006/04/01 · crossref published 2006/04/01 · crossref published-print 2006/04/01 · openalex publication_date 2006/04/01 · crossref published-online 2006/04/02 · crossref created 2006/04/02 · crossref deposited 2023/05/18 · openalex created_date 2025/10/10 · crossref indexed 2026/07/28 · openalex updated_date 2026/07/28

Citations

• 子ども支援のための教師へのコンサルテーションに関する研究 : 効果的なコンサルテーションスキルの観点から(X 教育心理学関係 博士論文要旨)

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• Lineage- and stage-restricted lentiviral vectors for the gene therapy of chronic granulomatous disease
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• Effective Gene Therapy of Mice with Congenital Erythropoietic Porphyria Is Facilitated by a Survival Advantage of Corrected Erythroid Cells
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• Gene therapy clinical trials worldwide to 2012 – an update
• Gene therapy [wikipedia]