J Muenzer

1. Intrathecal idursulfase‐ IT in children younger than 3 years with neuronopathic mucopolysaccharidosis II in a single‐arm, open‐label, phase 2/3 substudy and extension
   2026/02/22 by J Muenzer, Barbara K. Burton, Paul R. Harmatz +12 · 1 voice
   Medicine · #Glycogen Storage Diseases and Myoclonus #Infant Development and Preterm Care #Lysosomal Storage Disorders Research