Eugen Mengel

1. Efficacy and safety of arimoclomol in Niemann‐Pick disease type C: Results from a double‐blind, randomised, placebo‐controlled, multinational phase 2/3 trial of a novel treatment
   2021/08/21 by Eugen Mengel, Marc C. Patterson, Rosalia Maria Da Riol +26 · 3 citations
   Chemistry · Medicine · #Autoimmune and Inflammatory Disorders Research #Carbohydrate Chemistry and Synthesis #Lysosomal Storage Disorders Research