Cynthia C. Bartholomae

1. Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
   2009/11/05 by Nathalie Cartier, Salima Hacein‐Bey‐Abina, Cynthia C. Bartholomae +23 · 13 citations
   Biochemistry, Genetics and Molecular Biology · Medicine · #Virus-based gene therapy research #Peroxisome Proliferator-Activated Receptors #Neurogenetic and Muscular Disorders Research
2. Genome Sequencing of SHH Medulloblastoma Predicts Genotype-Related Response to Smoothened Inhibition
   2014/03/01 by Marcel Kool, David Jones, Natalie Jäger +73 · 1 citation
   Biochemistry, Genetics and Molecular Biology · #Hedgehog Signaling Pathway Studies #Genomics and Chromatin Dynamics #Chromatin Remodeling and Cancer