Harry L. Malech

1. Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency
   2021/05/11 by Donald B. Kohn, Claire Booth, Kit L. Shaw +50 · 2 citations
   Biochemistry, Genetics and Molecular Biology · #Virus-based gene therapy research #Adenosine and Purinergic Signaling #Biochemical and Molecular Research
2. STAT3 Mutations in the Hyper-IgE Syndrome
   2007/09/19 by Steven M. Holland, Frank R. DeLeo, Houda Zghal Elloumi +22 · 1 citation
   Immunology and Microbiology · Health Professions · #Immunodeficiency and Autoimmune Disorders #T-cell and B-cell Immunology #Pediatric health and respiratory diseases
3. Lentiviral Gene Therapy Combined with Low-Dose Busulfan in Infants with SCID-X1
   2019/04/17 by Ewelina Mamcarz, Sheng Zhou, Timothy Lockey +28 · 1 citation
   Biochemistry, Genetics and Molecular Biology · Medicine · Immunology and Microbiology · #Virus-based gene therapy research #CAR-T cell therapy research #Immunodeficiency and Autoimmune Disorders
4. An Emerging Era of Clinical Benefit From Gene Therapy
   2015/04/21 by Harry L. Malech, Hans D. Ochs · 1 citation
   Biochemistry, Genetics and Molecular Biology · Medicine · #CAR-T cell therapy research #CRISPR and Genetic Engineering #Virus-based gene therapy research