Chiho Ono
- Long‐Term Efficacy and Safety of Glycerol Phenylbutyrate in Japanese Patients With Urea Cycle Disorders: Results From a Phase 3 Switch‐Over and 12‐Month Extension Study
2026/06/14 by Yoichi Wada, Mahoko Furujo, Kenichi Kashimada +10 · 1 voice
Biochemistry, Genetics and Molecular Biology · Medicine · #Adverse effect #Dialysis and Renal Disease Management #Discontinuation #Genomics and Rare Diseases #Glutamine #Metabolism and Genetic Disorders #Metabolite #Pharmacokinetics #Phenylbutyrate #Urea #Urea cycle