Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial

2014/01/15 by Robert E MacLaren, Robert E. MacLaren, Markus Groppe +22 · 1 citation
Biochemistry, Genetics and Molecular Biology · Neuroscience · #Photoreceptor and optogenetics research #Retinal Development and Disorders #Virus-based gene therapy research

paper · pdf · doi:10.1016/s0140-6736(13)62117-0

openalex publication_date 2014/01/15 · crossref created 2014/01/15 · crossref issued 2014/03/01 · crossref published 2014/03/01 · crossref published-print 2014/03/01 · crossref deposited 2018/10/07 · openalex created_date 2025/10/10 · crossref indexed 2026/07/30 · openalex updated_date 2026/07/30

Citations

• AAV2-GAD gene therapy for advanced Parkinson's disease: a double-blind, sham-surgery controlled, randomised trial
• Vision 1 Year after Gene Therapy for Leber's Congenital Amaurosis
• Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis
• Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial

Cited by

• Gene therapy [wikipedia]