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What is the research question? Estimands explained

2025/03/01 by Rolf H. H. Groenwold, Saskia le Cessie, Olaf M. Dekkers · 1 voice
Economics, Econometrics and Finance · #Health Systems, Economic Evaluations, Quality of Life

paper · doi:10.1093/ejendo/lvaf048

openalex publication_date 2025/03/01 · openalex created_date 2025/10/10 · openalex updated_date 2026/07/31

Abstract

Although many papers of medical research report on a treatment effect, it is not always clear what is exactly meant by that effect. An estimand is a precise definition of a treatment effect and includes 5 attributes: population, treatment, (outcome) variable, intercurrent events, and summary measure. In this paper, we discuss how the estimand framework helps to align different phases of studies of medical treatments, from research objectives to design, conduct, analysis, and reporting of results.

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