Sustained Therapeutic Reversal of Huntington's Disease by Transient Repression of Huntingtin Synthesis

2012/06/01 by Holly Kordasiewicz, Holly B. Kordasiewicz, Lisa M. Stanek +20 · 4 citations
Biochemistry, Genetics and Molecular Biology · Neuroscience · #Genetic Neurodegenerative Diseases #Mitochondrial Function and Pathology #Muscle Physiology and Disorders

paper · pdf · doi:10.1016/j.neuron.2012.05.009

openalex publication_date 2012/06/01 · openalex created_date 2025/10/10 · openalex updated_date 2026/07/31

Citations

• A YAC Mouse Model for Huntington’s Disease with Full-Length Mutant Huntingtin, Cytoplasmic Toxicity, and Selective Striatal Neurodegeneration

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