Huntington’s disease treated for first time using gene therapy

2025/09/25 by Elie Dolgin · 1 voice · 9 citations
Neuroscience · Biochemistry, Genetics and Molecular Biology · Medicine · #Genetic Neurodegenerative Diseases #Mitochondrial Function and Pathology #Neurological disorders and treatments

paper · doi:10.1038/d41586-025-03139-9

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Discussions

• 🚨 TWO great news in medical science 🧪 1️⃣ A gene therapy targeting Huntington's Disease has shown significant success in a small clinical trial by slowing down the progression of the disease. (1/2 [bsky, 32 points, 1 comments]